Families Fight for a Muscular Dystrophy Drug’s Approval
Children play on a playground beneath a movie screen at the Georgetown Drive-In movie theater in Georgetown, Indiana, U.S., on Friday, July 17, 2015.
Photographer: Bloomberg/BloombergHi, it’s Angelica in Boston. Families are pleading with the FDA to approve a gene therapy for a debilitating genetic disease. But first…
Sheila Ungerer started noticing something was amiss with her son Will when he was 3 years old. He couldn’t jump with both feet, which she thought might just be a developmental delay.